Casgevy sickle cell gene therapy is now FDA-approved for children as young as two, opening access for 5,500 more U.S. kids.
CRISPR Therapeutics wins FDA pediatric approval for Casgevy, boosting market potential and pipeline upside despite slow uptake. Click here to read more.
The FDA on Wednesday expanded the approval for exagamglogene autotemcel (exa-cel, Casgevy) in severe sickle cell disease with ...
July 1 (Reuters) - The U.S. Food and Drug Administration approved expanded use of Vertex Pharmaceuticals' gene therapy in ...
In patients with fibrodysplasia ossificans progressiva, an oral selective inhibitor of activin receptor–like kinase 2 was ...
I’m currently in the final stages of recovering from osteonecrosis of the jaw (ONJ). Getting a diagnosis took two months, all ...
The chronic loss of joint cartilage known as osteoarthritis causes pain and bone decay for hundreds of millions of people ...
The U.S. Food and Drug Administration today issued a supplemental approval for Casgevy (exagamglogene autotemcel) for ...
Orca Bio, a commercial-stage biotechnology company committed to transforming the lives of patients through high-precision cell therapy, today announced the U.S. Food and Drug Administration (FDA) has ...
Manuel, stars of TLC's "Jay & Pamela," candidly discuss living with OI Type III, ahead of the series' Season 2 premiere.
Advanced analytical methods integrating clinical trial and real-world data address key evidence gaps in rare, difficult-to-treat blood cancers ...
Below are summaries of recent Fred Hutch Cancer Center research findings, patient stories and other news. If you’re interested in reporting on any of this month’s stories, contact media@fredhutch.org ...
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